Rare disease patients priced out of drugs market

The 1992 Hollywood movie "Lorenzo’s Oil," depicts the true story of Lorenzo, a five-year-old boy who suffered from adrenoleukodystrophy (ALD), a rare and incurable disease that slowly destroys the entire nervous system. The movie showed how Lorenzo’s grave physical and mental decline was finally stopped when his tireless parents found a treatment based on a mixture of oils, despite skepticism from doctors. The film illustrated perfectly the struggle faced by patients suffering from any of 6,000 known rare conditions worldwide, generally known as orphan diseases

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